NP CANADA FUNDED RESEARCH

Niemann-Pick Canada is proud to be supporting the following research grants. Please reach out to us directly to learn more about this exciting science that we know will contribute towards advancing knowledge into Niemann-Pick diseases and future therapies: 

Dr. Ronald Cohn, MD
The Hospital for Sick Children, Toronto Ontario Canada
Using Genome Editing to Understand and Treat NiemannPick Type C Disease 
December 2019 – December 2021 

Dr. Kevin T. Vaughan
University of Notre Dame, Notre Dame Indiana USA
Direct Stimulation of StARD9 as a Novel Therapeutic Strategy for NiemannPick Type C
December 2019 – December 2021

Dr. Mark Schultz, Ph.D
Department of Pathology, University of Michigan Medical School
Interrogating NPC1 Proteostasis
June 1, 2021 – June 1, 2023

CLINICAL TRAILS:

CLINICAL TRAILS:

Clinical Trials: 

Please visit the link below ClinicalTrials.gov and search for Niemann Pick Disease (type A, B, or C) for a list of privately and publicly funded clinical studies conducted around the world.  

https://clinicaltrials.gov 

INTERNATIONAl
NIEMANN-PICK
DISEASE REGISTRY (INPDR)

Patient registries are important within disease communities to gain knowledge and insight into disease processes, improve research and to improve diagnosis, treatment and care of those with certain diseases. This is particularly important with ultra-rare diseases such as Niemann-Pick diseases. 

Please consider joining the International Niemann-Pick Disease Registry (INPDR)  and share your experience of living with Niemann-Pick disease to support these advancements. 

Niemann-Pick Canada has partnered with INPDR to support recruitment of patient enrollment in this registry across Canada. 

To learn more, please visit their website https://inpdr.org or reach out to Niemann-Pick Canada directly should you have any questions or need support to enroll.

JOIN US IN OUR FIGHT FOR A CURE

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